The age of RNA interference drugs has arrived.
Alnylam Pharmaceuticals announced positive results Wednesday from a closely watched phase 3 clinical trial of patisiran, the company’s lead drug designed to treat a rare nerve disorder known as familial amyloid polyneuropathy (FAP.)
Seems a very small market(10,000) as I read it. Won’t the cost to consumer be astronomical! Happy for victims of FAP however.
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