An old, formerly inexpensive drug called Firdapse was just slapped with a steep new price tag: $375,000.
The Food and Drug Administration approved Firdapse late last month to treat a rare, neuromuscular disorder called Lambert-Eaton myasthenic syndrome. Although it’s the first approved therapy for this disease in the U.S., there’s a catch: For years, hundreds of patients have been receiving an unapproved version of this drug for free.
That’s because Catalyst Pharmaceuticals, the maker of Firdapse, did not actually invent the drug. Rather, a chemical called 3,4-DAP was found in the 1980s to improve symptoms of LEMS. It’s been used, off-label, ever since in the U.S. Catalyst, however, has spent the past several years testing a slightly modified version of 3,4-DAP in clinical trials, and secured approval — and market exclusivity for the next seven years.
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Hello,
I just wanted to read this article about Firdapse not get tricked into paying for something I don’t want. For sure you I would forget to cancel in the 30 days and even so I have given you my MC details. I am opposed to that.
This article is of interest to me. I appreciate the commercial model of STAT but there has to be a better way for you to capture your intended audience than this.
Sincerely,
Richard King
THIS IS NOT STRANGE NOR SURPRISING AS I HAVE REPEATEDLY STATE OVER AND OVER AGAIN FOR A MILLION TIMES OR MORE THE PHARMACEUTICAL EMPIRES ARE THE ONES IN CHARGE OF THE HEALTH CARE SYSTEM OR INDUSTRY IN THE UNITED STATES OF AMERICA .THIS IS JUST ONE MORE PRIME EXAMPLE .THANK YOU MORE TO COME
Interesting change in perspective. When I was a kid, 93 years ago, our family doctor, who came to our house to treat us, did his best to make us well. He carried his meds in a black leather bag. He died almost broke. Let that be a lesson. A lifetime supply of expensive drugs to make the patients feel better will make a lot of people well-off, patient excepted. We need more discussions about drug prices. Forget about illness research. More work on palliatives.
Congress should allow patients to buy pharmaceutical drugs from Canada and Europe. Let cut them out.
This is not a cure, so why is it not getting worse publicity than Gilread’s Yescarta, which is a really a cure and save lives for about the same price??
THIS IS ONLY ONE MORE PRIME EXAMPLE AS TO WHAT I HAVE WRITTEN EXTENSIVELY AND FREQUENTLY AS THE ISSUE OR MOST CRITICAL AND URGENT AT EVERY LEVELS OF HUMANITY AND LIFE ,NONE OTHER THAN THE HEALTH CARE SYSTEM AND OR INDUSTRY .BOTH HERE IN THE UNITED STATES OF AMERICA .THE POWER BROKER OF THE WORLD DUE TO THE FACT THAT WE OR SHOULD I SAY THE UNITED STATES OF AMERICA IS THE ONLY NATION AND OR COUNTRY THAT IS ABLE TO USE AN INSTITUTION SO NAMED THE FEDERAL RESERVE TO PRINT MONEY WITH ANY VALUE OR EARNINGS BY NATURAL PRODUCTIONS OR EARNINGS . THIS IS AGAIN WHY THE U.S.A IS TITLED THE MOST POWERFUL NATION . DUE TO IT? MILITARY AND ECONOMIC MIGHT . . WELL YES ECONOMIC MIGHT . HOWEVER . THE DEFICIT FOR THIS YEAR OF 2018 IS SEVEN HUNDRED SEVENTY NINE BILLION DOLLARS AND COUNTING AND THE DEBT OVER ALL IS TWENTY ONE TRILLION DOLLARS AND ALSO COUNTING EVERY DAY . CHINA IS THERE . THE ONLY REASON THEY ARE IN SECOND PLACE IS SIMPLY BECAUSE CHINA IS COMMUNIST , AND NOT A DEMOCRACY SYSTEM AS COMPARABLE TO WE THE U.S. A . I HAVE COMPILED THE AFOREMENTIONED SO AS TO POSE AND SET IN MOTION WITH ALL OF THE MONEY AND OR FUNDS THAT WE THE U.S .A HAVE WHETHER EARNED OR NOT . WE SPEND SO MUCH ON HEALTH CARE ALONE TRILLIONS IN THIS YEAR OF 2018 . I SAY FOUR TRILLION DOLLARS . AS IN THE YEAR OF 2017 THE SUM WAS THREE POINT FIVE TRILLION DOLLARS . SEVENTEEN POINT SEVEN PERCENT OF THE .G.D.P .THE GROSS DOMESTIC PRODUCT YET STILL WE HAVE THE WORST HEALTH SYSTEM AND RESULTS EVERY YEAR . NOTWITHSTANDING ALL OF THIS .WE HAVE THE ELITES .LIBERALS RADICALS . EMPERORS .MESSIAHS, GOD HEADS . THE MAIN STREAM MEDIA OF THE FOURTH ESTATE . AND THIS ONE IS THE NEW YORK TIMES AS THE GOLIATH AND SOME INTELLECTUALS TELLING THE UNREAD ,UNEDUCATED , UNIFORMED AND UNCARING THAT CLIMATE CHANGE AND OR GLOBAL WARMING IS THE DEATH NEAL . ABSOLUTE FALSE AND A CRIME OF INDOCTRINATION .MANIPULATION AND MISINFORMATION BY ALL OF THE CLIQUES I HAVE DOCUMENTED HERE ABOUT CLIMATE CHANGE AND GLOBAL WARMING .I WILL EXPAND AND ADDRESS THESE CONTINUALLY AS WE MOVE FORWARD FOR THE LONG AND LASTING JOURNEY OF THE TRUTH . THIS TRUTH IS THE NATURAL AND REAL TRUTH .UNLIKE THE ONES THAT THE NEW YORK TIMES . PRINT IN IT.?> PUBLICATIONS NEWSPAPER FOR WHICH I READ DAILY SO AS TO BE ABREAST WITH ALL THAT THE NEW YORK TIMES AND OTHERS OF THE MAIN STREAM MEDIA OF THE FOURTH ESTATE GIVE OUT . TO MISLEAD AND FRABRICATE A SIGNIFICANT OF THE POPULACE . . DUE TO THE REALITY THAT THE MAIN STREAM MEDIA IS WELL AWARE THAT THESE HUMANS ARE UNINFORMED AND EVEN MORE SIGNIFICANT THEY DO NOT READ . FOR INSTANCE .WE HAVE THE UNITED NATIONS CLIMATE CHANGE FALSE REPORTS . COMPRISING OF NEARLY SEVEN HUNDRED PAGES OF STATEMENTS AND DATA SO COMPILED BY THE NOBLE LAURETS AND SCHOLARS OF ESTEEM . FOR WHICH THEY ARE WELL AWARE THEY CAN DO SO AND GET AWAY WITH MURDER . IN OTHER WORDS .,THEY GENERALLY AND LITERALLY GO UNCHALLENGE . TREVOR MERCHANT .
Gibberish
TREVOR .A MERCHANT (sic) must be a comment bot, intended to stir up the pot? No one’s ideas can be quite that confused. Don’t fall prey to such jumbled garbage.
RE THE COMMENT MADE BY RKS, GIBBERISH ON FEBRUARY 06, 2019. WITH REGARDS TO MY COMMENT MADE . I WILL BRIEFLY .RESPOND TO THIS PERSON WITH .SAYING KNOWLEDGE IS POWER AND THE SHARING OF KNOWLEDGE TRUTHFULLY IS EMPOWERMENT . TO QUOTE .UNQUOTE . I DO NOT NEED TO RELY ON ANY MEDIA AND OR INSTITUTION FOR WHAT I HAVE WRITTEN . I WRITE AND SPEAK WITH AUTHORITY . BASE ON PERSONAL EXPERIENCE AND WITNESS THERE OFF . FIRSTLY MY MOTHER , AND MY BROTHER .,WHO WAS ONLY ADMITTED TO THE ALBERT EINSTIEN JACK WEILI ,MONTEFIORE CHAIN HOSPITAL IN THE BRONX .,NEW YORK CITY , FIVE WEEKS [5] AGO .I WERE THE PERSON WHO ACCOMPANIED HE THERE AND WERE PRESENT FOR NEARLY SIX HOURS [6] BEFORE I DEPARTED THIS DEATH CHAMBER S PRIMARILY IN THE EMERGENCY ROOMS ., THIS WAS THE SECOND TIME I HAD TO GO THERE WITH MY BROTHER WITHIN THE TIME FRAME OF THREE MONTHS A HE FELL THE FIRST TIME ON A SUNDAY AFTER NOON CHASING AFTER A NEW YORK CITY BUS . YES ON THIS TIME HE HAD TO WAIT NINE [9] HOURS BEFORE HE WAS ATTENDED TO . MY MOTHER WAS ADMITTED THERE DUE TO MY BROTHER BEING THE PROXY , MY MOTHER STATED AND COMMUNICATED FIRMLY AFTER THIS VISIT THAT SHE DID NOT INTEND OR WISH TO RETURN TO ANY HOSPITAL .EIGHTEEN MONTHS [18] MONTHS BEFORE MY BROTHER MADE HE GO THERE AGAIN FOR THE FINAL TIME . THEY KEPT HER THERE FOR ELEVEN [11] DAYS THEN SEND HER HOME TO DIE FIVE [5] DAYS AFTER, YES I VISITED MY MOTHER EVERY EVENING DURING VISITING HOURS FOR THE ELEVEN DAYS AND WITNESSED THE CHAOS AND BATTLED OF INFERIORITY AND CRISIS . SO . I AM NOT AFRAID TO INCLUDE AND OR STATE MY NAME AND OTHER SUCH INFORMATION . LIKE THIS PERSON WHO IS ANGRY AND BORING .I AM WELL AWARE THAT HE OR SHE HAS THE RIGHT UNDER THE FREEDOM OF SPEECH IN THIS NATION TO WRITE AND SPEAK AS HE OR SHE LIKES . HOWEVER DO NOT ATTACK ANY ONE .BASED ON THE TRUTH . . ,MORE TO COME . TUESDAY , FEBRUARY . 12, 2019 AT 3.49 P.M EASTERN STANDARD TIME . NEW YORK CITY ,