Patients are about to be enrolled in the first study to test a gene-editing technique known as CRISPR inside the body to try to cure an inherited form of blindness.
People with the disease have normal eyes but lack a gene that converts light into signals to the brain that enable sight.
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My daughter can see only light an can identify colours after she was.three years.she is now 26 yrs old.
Please advise how/ where recruitment is. Our son was diagnosed with Lebers Amaurosis at 4 months old. He is now 35 years old, lives and works in Los Angeles. Thank you, Teresa Marositz- parent