Skip to Main Content

People with severe beta-thalassemia who live in Europe have been denied access to Bluebird Bio’s approved gene therapy after the company withdrew it from the market last April. European health systems balked at the nearly $2 million price tag for the gene therapy called Zynteglo, and when negotiations broke down, Bluebird walked away.

But Saturday, Bluebird relied largely on European patients enrolled in its beta-thalassemia clinical trials to demonstrate the successful, long-term durability of Zynteglo. The juxtaposition is awkward for Bluebird, showing business priorities don’t always align with the biotech’s “patients first” mantra.

Unlock this article by subscribing to STAT+ and enjoy your first 30 days free!


Create a display name to comment

This name will appear with your comment