Skip to Main Content

In an unusual move, Sen. Bernie Sanders (I-Vt.) asked federal regulators to allow a small drug maker and compound pharmacies to resume supplies of a rare-disease treatment. And he cited patient complaints over pricing by Catalayst Pharmaceuticals (CPRX), which recently won regulatory approval for its own version and seven years of exclusive marketing that legally permits it to preclude sales of older, competitive medicines.

The move is the latest effort by the lawmaker to confront Catalyst, which now sells a drug to treat Lambert-Eaton myasthenic syndrome, or LEMS. Until December, patients could obtain an unapproved version for free from Jacobus Pharmaceuticals, a small, family-run company, thanks to a compassionate use program overseen by the Food and Drug Administration.

Unlock this article by subscribing to STAT+ and enjoy your first 30 days free!

GET STARTED