rare disease
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When even soft noises feel like a knife to the eardrums
Millions of Americans carry the sickle cell trait, many without knowing it. Could they be at risk for severe Covid-19?
I have spinal muscular atrophy. Critics of the $2 million new gene therapy are missing the point
Ten years after the ‘Berlin patient,’ doctors announce a second person has been effectively ‘cured’ of HIV
Their tissue turns to bone. Their joints freeze in place. And, finally, their hopes for treatment may be realized
‘Frustrated and panicking’: For some rare disease patients, shortages of protective gear pose a continued threat
