Biotech Adam Feuerstein Bluebird Bio’s gene therapy for blood disorders yields some impressive results ― but also raises questions
In the Lab Karen Weintraub Two newborn deaths in the same family set off a race to solve a medical mystery
First Opinion Christopher Anselmo How a blood test changed my life and helped me become a rare disease advocate
Business Dylan Scott This biotech company is trying to make a rare disease drug cheaper. Will it work?